07/20/2024
Ada and Lily, "thal-pals" with beta thalassemia, are on a groundbreaking journey with gene therapy at UCSF Benioff Children's Hospitals. Learn how they became the first patients on the West Coast to receive a treatment that could free them from lifelong transfusions.
Two sisters are receiving a breakthrough, FDA-approved treatment for beta thalassemia at UCSF Benioff Children's Hospital, Oakland. This is the first real therapy other than monthly transfusions for a devastating disease that destines people to shorter lives.