Contact information, map and directions, contact form, opening hours, services, ratings, photos, videos and announcements from PTC Therapeutics, Pharmaceutical Company, Piscataway, NJ.
PTC is a patient-centered biopharmaceutical company focused on discovering, developing & commercializing medicine for children and adults living with rare disease.
06/28/2025
Today we proudly recognize International PKU Day, led by ESPKU as a day to spread awareness and education about living with and highlight the many . A major aspect of living with PKU is dietary management, which impacts quality of life, from childhood through adulthood. For many, the journey involves navigating the complexities of medical formulas and the social dynamics of food-related gatherings.
At PTC, we believe innovation thrives when everyone has a seat at the table and feels seen, heard and valued. This month, as we recognize both and , we’re proud to highlight the many ways our workplace culture is built on empathy, authenticity and unity. We’re committed to creating a space where everyone can bring their full self to work.
Learn more about how we are putting these values into action: https://bit.ly/4458n3o
06/13/2025
Recently our team spent an inspiring weekend learning and connecting with families and the PKU community at the flok Family Camp West in Oregon. Whether it was sharing meals, swapping stories, attending science night, or joining in on the flok Olympics field games and other fun events, we were proud to support the community in their journey living with a rare condition like .
06/05/2025
🌎 This , we’re celebrating the power of collective action—and our global teams’ commitment to creating a greener future.
🌳 From planting nearly 400 climate-resilient trees in Switzerland to contributing to reforestation in Spain, PTC teams are making meaningful change in their local communities. These efforts are just part of our broader commitment to environmental stewardship and sustainability across the company.
As we approach the end of Friedreich’s Ataxia (FA) Awareness Month, we’re honored to continue raising awareness for this genetic, progressive neuromuscular disease that mainly affects the central nervous system and the heart by sharing Alex's story. As a patient advocate with the Freidreich's Ataxia Research Alliance (FARA) FA Ambassador program, Alex hopes to help others better understand the realities of this condition and inspire strength in the community to keep moving forward.
We're proud to support Huntington's Disease (HD) Awareness Month by amplifying the voices of those living with this rare inherited disorder. Listen in as Evonne shares her experience with , offering honesty, strength and perspective to help others better understand the condition and its impact. Learn more about her story and message to the HD community: https://bit.ly/4dpmmFB
05/12/2025
For Friedreich’s Ataxia (FA) Awareness Month, we’re proud to spotlight Andrea—a proud advocate of the community. By sharing her personal journey, Andrea helps raise awareness of FA and brings visibility to the everyday experiences of living with a . We thank Andrea for her courage and her commitment to spreading awareness. Learn more about her story and message to the FA community: https://bit.ly/4iSJtJB
04/23/2025
Behind every breakthrough there are brilliant scientists, groundbreaking ideas, and the labs where it all begins.
This , we're proud to celebrate our science and research teams, whose unique expertise enables us to discover and advance innovative therapies.
04/14/2025
Emma Decker lives with phenylketonuria ( ), a rare, inherited metabolic disorder that requires lifelong management. For Emma, staying on top of her PKU isn’t just about diet – it’s about maintaining control and finding ways to help others in the community.
At PTC Therapeutics, we know that every PKU journey is different, which is why listening to the community is at the heart of what we do. Emma’s story is a powerful reminder of the resilience and determination that define so many living with .
Learn more about Emma’s experience and how we’re working to support the PKU community: https://bit.ly/42eftTE
04/02/2025
We work to pioneer innovative treatments for patients around the world. As a part of these efforts, we are proud to share that our gene therapy for AADC deficiency has received regulatory approval for eligible patients in Hong Kong.
03/24/2025
Our teams were thrilled to connect with the Friedreich's ataxia (FA) community while attending the 2025 MDA Clinical & Scientific Conference in Dallas last week and share data from our FA program. We are proud to be developing a potential treatment for children and adults living with this rare disorder.
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Everyone has a different definition of progress. For the last 20 years, we’ve measured our progress researching rare disease in moments. Smiling ones and crying ones. Moments spent with our patients’ families and ones with their friends. We know that every step forward comes after several steps backward, because we’ve lived it—whether spending time with families in their homes or with our scientists researching in our labs in central New Jersey.
It can be easy to lose yourself as you progress further. Although we’ve grown, our heart remains in the same place, because we’ve never measured ourselves like larger companies do. Our biggest accomplishment has always been the time we can give to all of our families. Whether it’s hours, days, months, or years, every small moment is a big win.
COMMUNITY GUIDELINES
Thank you for your interest in PTC Therapeutics. We’re happy you’re here! This Page is a place for community members to engage with us, learn about our corporate initiatives and programs, and participate in an open dialogue with other members of the PTC and rare disease communities.
We recognize the importance of the rights of individuals to voice their opinion on social media and find community. In order to ensure that these communications are positive and productive, we’ve created the following guidelines.
Please share your thoughts with us! We want to hear from you and we’ll respond to your questions and comments as soon as possible.
Please keep in mind this Page is intended for US audiences only and not intended for medical advice.
Keep comments relevant and on-topic, and stay positive.
Due to regulations that govern the healthcare industry, we may choose to not engage in sensitive topics or talk about any pharmaceutical products or other health treatments on our Page. Reminder: All communications regarding PTC products must be reviewed and approved in advance by the review committee to ensure compliance with FDA requirements. All claims and communications about PTC products must be consistent with the FDA-approved label.
PTC Therapeutics reserves the right to not respond to, remove or hide any comments, posts, photos, or videos shared on the Page that are inappropriate, misleading, abusive or defamatory. In addition, we respectfully request that you avoid posting comments that include:
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There may be other instances that will require us to remove a comment and we will let you know why if we do.
The content posted on this Page is intended to inform you. It is not intended to be a substitute for professional medical advice, diagnosis or treatment. Please always consult your doctor.
PTC Therapeutics reserves the right to delete any posting at its sole discretion.
